The FDA on Friday approved a new spinal muscular atrophy drug that patients can take at home.
Risdiplam (Evrysdi) is a liquid medicine intended for daily use that was developed by Roche subsidiary Genentech in partnership with the SMA Foundation and South Plainfield, NJ-based PTC Therapeutics (NASDAQ: PTCT).
Regulators OK’d the drug, intended for daily administration via mouth or feeding tube, for patients with all forms of the disease starting at two months of age. In a prepared statement the FDA’s Billy Dunn, who heads its neuroscience unit, highlighted the dosing advantage.
“Evrysdi is the first drug for this disease… Read more »
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